Orkin, S. H. Nature Rev. Genet. 1, 57–64 (2000).
Agarwal, P. et al. Nature https://doi.org/10.1038/s41586-025-08938-8 (2025).
Jaiswal, S. et al. N. Engl. J. Med. 371, 2488–2498 (2014).
Genovese, G. et al. N. Engl. J. Med. 371, 2477–2487 (2014).
Xie, M. et al. Nature Med. 20, 1472–1478 (2014).
Weeks, L. D. & Ebert, B. L. Blood 142, 2235–2246 (2023).
Weeks, L. D. et al. N. Engl. J. Med. Evid. https://doi.org/10.1056/EVIDoa2200310 (2023).
Pasupuleti, S. K. & Kapur, R. Curr. Opin. Hematol. 31, 193–198 (2024).
Belizaire, R., Wong, W. J., Robinette, M. L. & Ebert, B. L. Nature Rev. Immunol. 23, 595–610 (2023).
Zhang, C. R. C. et al. Exp. Hematol. 80, 36–41 (2019).
Zhou, P. et al. Nature 561, 122–126 (2018).
Peled, J. U. et al. N. Engl. J. Med. 382, 822–834 (2020).
Ryzhakov, G. Nature Commun. 9, 3797 (2018).